Rescue of a Mouse Model of Spinal Muscular Atrophy With Respiratory Distress Type 1 by AAV9-IGHMBP2 Is Dose Dependent.
published in: Molecular Therapy
date of publication: 2016-02-10
main subject: spinal muscular atrophy, muscular atrophy
Cites articles 33
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Article - wd:Q30761984