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Therapeutic levels of fetal hemoglobin in erythroid progeny of β-thalassemic CD34+ cells after lentiviral vector-mediated gene transfer

লেখক

Andrew Wilber

এতে প্রকাশিত: Blood

তারিখে প্রকাশিত: 2010-12-14

ভাষা: ইংরেজি ভাষা

Cites articles 44

তারিখ

শিরোনাম

লেখকগণ

2010-05

Lentiviral vector gene therapy: effective and safe?
2010-04-01

Transcriptional silencing of {gamma}-globin by BCL11A involves long-range interactions and cooperation with SOX6.
2010-02-26

A zinc-finger transcriptional activator designed to interact with the gamma-globin gene promoters enhances fetal hemoglobin production in primary human adult erythroblasts

Andrew Wilber, Carlos Barbas
2009-12-01

Gene therapy. Beta-thalassemia treatment succeeds, with a caveat.

Jocelyn Kaiser
2009-04-13

Amelioration of murine beta-thalassemia through drug selection of hematopoietic stem cells transduced with a lentiviral vector encoding both gamma-globin and the MGMT drug-resistance gene
2009-05

Ineffective erythropoiesis and thalassemias
2009-02-17

Optimized lentiviral vector design improves titer and transgene expression of vectors containing the chicken beta-globin locus HS4 insulator element
2008-12-04

Human fetal hemoglobin expression is regulated by the developmental stage-specific repressor BCL11A.

Hanna K. A. Mikkola, Joel N Hirschhorn
2008-12-02

Correction of murine sickle cell disease using gamma-globin lentiviral vectors to mediate high-level expression of fetal hemoglobin
2008-11-11

Artificial microRNAs as siRNA shuttles: improved safety as compared to shRNAs in vitro and in vivo

Ryan L. Boudreau
2008-07-23

In vivo selection of genetically modified erythroblastic progenitors leads to long-term correction of beta-thalassemia

Michael N Antoniou
2008-03-04

Physiological promoters reduce the genotoxic risk of integrating gene vectors

Axel Schambach, Daniela Zychlinski, Ute Modlich, Tobias Maetzig
2008-03-01

Globin Lentiviral Vector Insertions Can Perturb the Expression of Endogenous Genes in β-thalassemic Hematopoietic Cells,Globin lentiviral vector insertions can perturb the expression of endogenous genes in beta-thalassemic hematopoietic cells
2007-12-03

Hematopoietic cell transplantation for thalassemia and sickle cell disease: past, present and future
2007-11-26

Advances in the allogeneic transplantation for thalassemia
2006-09-01

Lessons from Nature: microRNA-based shRNA libraries

Gregory Hannon
2005-09-01

A lentiviral microRNA-based system for single-copy polymerase II-regulated RNA interference in mammalian cells

Gregory Hannon
2005-01-01

Bone marrow transplantation in adults with thalassemia: Treatment and long-term follow-up
2004-10-01

High-level beta-globin expression and preferred intragenic integration after lentiviral transduction of human cord blood stem cells

Richard Humphries, Philippe Leboulch, Connie Eaves, Suzan Imren, Mary E Fabry, Robert Pawliuk
2004-06-15

Extended beta-globin locus control region elements promote consistent therapeutic expression of a gamma-globin lentiviral vector in murine beta-thalassemia
2004-08-03

Successful correction of the human beta-thalassemia major phenotype using a lentiviral vector
2003-06-01

Bcl11b is required for differentiation and survival of alphabeta T lymphocytes,Bcl11b is required for differentiation and survival of αβ T lymphocytes

Yukio Mishima
2003-06-01

Bcl11a is essential for normal lymphoid development

Neal G. Copeland, Nancy A. Jenkins, Lino Tessarollo
2003-08-21

Correction of a mouse model of sickle cell disease: lentiviral/antisickling beta-globin gene transduction of unmobilized, purified hematopoietic stem cells
2003-05-01

Flow cytometric analysis of hydroxyurea effects on fetal hemoglobin production in cultures of beta-thalassemia erythroid precursors
2002-10-21

Permanent and panerythroid correction of murine beta thalassemia by multiple lentiviral integration in hematopoietic stem cells

Philippe Leboulch, Connie Eaves
2002-09-01

Development of virus vectors for gene therapy of beta chain hemoglobinopathies: flanking with a chromatin insulator reduces gamma-globin gene silencing in vivo
2002-10-31

The degree of phenotypic correction of murine beta -thalassemia intermedia following lentiviral-mediated transfer of a human gamma-globin gene is influenced by chromosomal position effects and vector copy number
2002-03-01

In vitro mass production of human erythroid cells from the blood of normal donors and of thalassemic patients

Angela Di Baldassarre, Roberta Di Pietro, Giovanni Migliaccio
2002-03-01

Comparison of various envelope proteins for their ability to pseudotype lentiviral vectors and transduce primitive hematopoietic cells from human blood
2001-12-01

Correction of sickle cell disease in transgenic mouse models by gene therapy
2001-04-01

Phenotype-genotype relationships in monogenic disease: lessons from the thalassaemias.

নিবন্ধ - wd:Q34707143

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